NasdaqGS:BEAMBiotechs
Beam Therapeutics (BEAM) Is Down 9.9% After Advancing BEAM-302 Into FDA Accelerated Approval Pathway
Earlier this week, Beam Therapeutics reported updated Phase 1/2 data for its in vivo base-editing therapy BEAM-302 in alpha-1 antitrypsin deficiency, selecting a 60 mg dose to advance into pivotal development under a potential FDA accelerated approval pathway.
The data highlight rapid, durable biomarker changes consistent with direct genetic correction in both lung and liver disease patients, underscoring BEAM-302’s potential as a one-time, base-editing treatment approach.
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