NasdaqGS:RAREBiotechs
Ultragenyx Priority Review For DTX401 Spurs Fresh Look At Valuation
Ultragenyx Pharmaceutical (NasdaqGS:RARE) announced that the US FDA has accepted its Biologics License Application for DTX401, a gene therapy for Glycogen Storage Disease Type Ia.
The FDA has granted Priority Review to the application, signaling an expedited assessment timeline.
If approved, DTX401 could become the first pharmacologic treatment option for people living with Glycogen Storage Disease Type Ia.
For Ultragenyx, with a current share price of $23.04, this regulatory milestone...