NasdaqGS:IONSBiotechs
How Zilganersen’s Positive Pivotal Data and FDA Priority Review Could Impact Ionis Pharmaceuticals (IONS) Investors
Ionis Pharmaceuticals recently reported additional positive results from its pivotal Phase 1-3 trial of zilganersen in Alexander disease, showing statistically significant stabilization of gait speed and broad symptom benefits over 60 weeks, with the drug currently under FDA Priority Review and a PDUFA decision date set for September 22, 2026.
Beyond motor endpoints, exploratory data showing reduced glial fibrillary acidic protein levels and consistently better patient- and...