NasdaqGS:BEAMBiotechs
The Bull Case for Beam Therapeutics (BEAM) Could Change Following Positive BEAM-302 Phase 1/2 Trial Results
Beam Therapeutics has announced results from its ongoing Phase 1/2 trial of BEAM-302 for alpha-1 antitrypsin deficiency, reporting well-tolerated, dose-dependent mutation correction and durable restoration of functional alpha-1 antitrypsin protein in 17 treated patients as of August 1, 2025.
Expansion into registrational development and the initiation of additional dose cohorts mark a potential shift for BEAM-302 as a possible single-course treatment for both liver and lung manifestations of...