ENXTBR:UCBPharmaceuticals
Is KYGEVVI’s FDA Approval Expanding UCB’s Innovation Narrative and Therapeutic Reach (ENXTBR:UCB)?
UCB announced that KYGEVVI, a combination therapy for thymidine kinase 2 deficiency (TK2d), has received approval from the U.S. FDA, making it the first and only approved treatment for this ultra-rare, life-threatening mitochondrial disorder in both adults and pediatric patients with symptom onset before age 12.
This approval provides UCB with entry into a new therapeutic area with high unmet need, and comes with a Rare Pediatric Disease Priority Review Voucher from the FDA, highlighting...