NasdaqGS:IONSBiotechs
Ionis FDA And Phase 3 Updates Reframe Rare Disease Valuation Story
Ionis Pharmaceuticals (NasdaqGS:IONS) received FDA Priority Review for olezarsen in severe hypertriglyceridemia, indicating an expedited regulatory timeline.
New Phase 3 analyses for DAWNZERA, an RNA targeted therapy for hereditary angioedema, are scheduled for presentation at a major scientific forum.
These developments focus on two rare disease programs that are central to Ionis’s drug development efforts.
Ionis Pharmaceuticals focuses on RNA targeted medicines, with a portfolio that...