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U.S. Pharmaceuticals & Biotech Top Growth Stocks

Results

44

3 new
According to our Simply Wall St analysis these are the best growth companies.. We look for companies with high forecasted growth and healthy balance sheets that can deliver sustained growth over the long term.
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44 companies

Axsome Therapeutics

Market Cap: US$11.6b

A biopharmaceutical company, develops and delivers novel therapies for the management of central nervous system (CNS) disorders in the United States.

AXSM

US$220.75

7D

6.8%

1Y

89.0%

Madrigal Pharmaceuticals

Market Cap: US$12.3b

A biopharmaceutical company, focuses on delivering novel therapeutics for metabolic dysfunction-associated steatohepatitis (MASH) in the United States.

MDGL

US$534.49

7D

-1.2%

1Y

25.6%

TG Therapeutics

Market Cap: US$7.6b

A commercial stage biopharmaceutical company, focuses on the acquisition, development, and commercialization of novel treatments for B-cell mediated diseases in the United States and internationally.

TGTX

US$53.89

7D

-3.7%

1Y

69.7%

Insmed

Market Cap: US$28.3b

Develops and commercializes therapies for patients with serious and rare diseases in the United States, Europe, Japan, and internationally.

INSM

US$129.41

7D

2.5%

1Y

-9.6%

Rhythm Pharmaceuticals

Market Cap: US$7.2b

A commercial-stage biopharmaceutical company, focuses on the rare neuroendocrine diseases in the United States and internationally.

RYTM

US$104.71

7D

1.9%

1Y

9.0%

Praxis Precision Medicines

Market Cap: US$9.3b

A clinical-stage biopharmaceutical company, engages in the development of therapies for central nervous system (CNS) disorders characterized by neuronal excitation-inhibition imbalance in the United States.

PRAX

US$334.58

7D

-4.9%

1Y

727.1%

Ardelyx

Market Cap: US$892.1m

Ardelyx, Inc. discovers, develops, and commercializes medicines to treat unmet medical needs in the United States and internationally.

ARDX

US$3.58

7D

-5.3%

1Y

-45.2%

Ionis Pharmaceuticals

Market Cap: US$9.0b

A commercial-stage biotechnology company, provides RNA-targeted medicines in the United States.

IONS

US$54.21

7D

-6.7%

1Y

-11.3%

Corcept Therapeutics

Market Cap: US$12.2b

A biopharmaceutical company, engages in the discovery and development of medications to treat severe endocrinologic, oncologic, metabolic, and neurologic disorders in the United States.

CORT

US$112.79

7D

1.0%

1Y

62.2%

Capricor Therapeutics

Market Cap: US$486.6m

A clinical-stage biotechnology company, engages in the development of transformative cell and exosome-based therapeutics for treating duchenne muscular dystrophy (DMD) and other diseases with unmet medical needs in the United States.

CAPR

US$8.37

7D

-11.0%

1Y

38.6%

Revolution Medicines

Market Cap: US$43.7b

A clinical-stage precision oncology company, develops novel targeted therapies for RAS-addicted cancers.

New

RVMD

US$203.77

7D

-3.0%

1Y

341.1%

Cellectar Biosciences

Market Cap: US$21.8m

A clinical biopharmaceutical company, focuses on the discovery, development, and commercialization of drugs for the treatment of cancer in the United States.

CLRB

US$2.31

7D

-2.5%

1Y

-55.1%

Aldeyra Therapeutics

Market Cap: US$80.8m

A biotechnology company, discovers and develops therapies designed to treat immune-mediated diseases.

ALDX

US$1.34

7D

-9.5%

1Y

-73.7%

CG Oncology

Market Cap: US$6.4b

A late-stage clinical biopharmaceutical company, develops and commercializes cretostimogene grenadenorepvec for patients with bladder cancer in the United States.

CGON

US$72.35

7D

-3.1%

1Y

109.1%

Nuvation Bio

Market Cap: US$2.1b

A clinical-stage biopharmaceutical company, focuses on developing product candidates for cancer treatment.

NUVB

US$6.07

7D

-10.9%

1Y

92.7%

Kiniksa Pharmaceuticals International

Market Cap: US$6.0b

A biopharmaceutical company, develops and commercializes medical therapies in the United States, the United Kingdom, and internationally.

KNSA

US$76.27

7D

-2.1%

1Y

108.6%

Eton Pharmaceuticals

Market Cap: US$1.6b

A pharmaceutical company, focuses on developing and commercializing treatments for rare diseases.

ETON

US$57.08

7D

-2.3%

1Y

221.0%

Arcutis Biotherapeutics

Market Cap: US$3.0b

A biopharmaceutical company, focuses on developing and commercializing treatments for dermatological diseases.

ARQT

US$23.89

7D

-0.06%

1Y

41.1%

AC Immune

Market Cap: US$274.4m

A clinical stage biopharmaceutical company, discovers, designs, and develops medicines, and therapeutic and diagnostic products for the prevention and treatment of neurodegenerative diseases associated with protein misfolding.

ACIU

US$2.76

7D

-3.5%

1Y

11.3%

Grace Therapeutics

Market Cap: US$46.7m

Engages in the development and commercialization of pharmaceutical products for rare and orphan diseases in Canada.

GRCE

US$2.22

7D

5.7%

1Y

-27.7%

Sol-Gel Technologies

Market Cap: US$215.9m

Together with its subsidiary Sol-Gel Technologies Inc., develops topical dermatological drugs for patients with severe skin conditions in Israel, China, Switzerland, Canada, the United States and internationally.

SLGL

US$65.94

7D

-5.1%

1Y

175.0%

Belite Bio

Market Cap: US$7.0b

A clinical stage biopharmaceutical drug development company, engages in the research and development of novel therapeutics with unmet medical needs in the United States.

BLTE

US$173.79

7D

-10.2%

1Y

160.2%

SIGA Technologies

Market Cap: US$217.7m

A commercial-stage pharmaceutical company, focuses on the health security market in the United States.

SIGA

US$3.03

7D

-7.9%

1Y

-66.3%

NewAmsterdam Pharma

Market Cap: US$2.7b

A late-stage biopharmaceutical company, develops therapies to enhance patient care in populations with cardiometabolic disease.

NAMS

US$22.80

7D

-10.2%

1Y

-5.5%

Vera Therapeutics

Market Cap: US$2.5b

A clinical stage biotechnology company, focuses on the development and commercialization of transformative treatments for patients with immunological diseases.

VERA

US$35.05

7D

-2.3%

1Y

44.6%

Aytu BioPharma

Market Cap: US$21.4m

A pharmaceutical company, focuses on commercializing novel therapeutics in the United States and internationally.

AYTU

US$1.99

7D

-10.0%

1Y

-14.6%

uniQure

Market Cap: US$3.1b

Develops treatments for patients suffering from rare and other devastating diseases in the United States.

QURE

US$44.51

7D

0.02%

1Y

200.0%

TriSalus Life Sciences

Market Cap: US$287.2m

Engages in the research, development, and commercialization of drug delivery technology platform and immuno-oncology therapeutics to improve outcomes for patients with difficult-to-treat liver and pancreatic cancers in the United States.

TLSI

US$4.67

7D

-6.7%

1Y

1.4%

AnaptysBio

Market Cap: US$1.6b

A clinical-stage biotechnology company, focuses in delivering immunology therapeutics for autoimmune and inflammatory diseases in the United States.

ANAB

US$53.87

7D

-5.2%

1Y

167.2%

Liquidia

Market Cap: US$6.0b

A biopharmaceutical company, develops, manufactures, and commercializes various products for rare cardiopulmonary diseases in the United States.

LQDA

US$66.74

7D

-2.8%

1Y

149.3%

Iovance Biotherapeutics

Market Cap: US$3.9b

A commercial-stage biopharmaceutical company, develops and commercializes cell therapies using autologous tumor infiltrating lymphocyte for the treatment of metastatic melanoma and other solid tumor cancers in the United States and internationally.

IOVA

US$8.60

7D

-2.2%

1Y

278.9%

Unicycive Therapeutics

Market Cap: US$147.4m

A clinical-stage biotechnology company, identifies, develops, and commercializes therapies for the treatment of kidney diseases in the United States.

UNCY

US$5.29

7D

2.5%

1Y

34.3%

Journey Medical

Market Cap: US$204.1m

A commercial-stage pharmaceutical company that focuses on the development and commercialization of pharmaceutical products for the treatment of dermatological conditions in the United States.

DERM

US$7.23

7D

-8.0%

1Y

1.5%

Compass Therapeutics

Market Cap: US$360.2m

A clinical-stage oncology-focused biopharmaceutical company, develops antibody-based therapeutics for the treatment of various human diseases in the United States.

CMPX

US$2.00

7D

-16.0%

1Y

-45.8%

Definium Therapeutics

Market Cap: US$5.2b

A clinical biopharmaceutical company, develops novel product candidates to treat brain health disorders.

DFTX

US$38.89

7D

2.1%

1Y

307.2%

Fennec Pharmaceuticals

Market Cap: US$384.3m

Operates as a commercial stage biopharmaceutical company in the United States.

FENC

US$10.96

7D

-11.5%

1Y

26.4%

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