Broad Approvals Will Elevate Rare Disease Markets Despite Setbacks

Published
21 Mar 25
Updated
14 Aug 25
AnalystConsensusTarget's Fair Value
US$68.31
28.7% undervalued intrinsic discount
14 Aug
US$48.70
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1Y
47.4%
7D
-3.3%

Author's Valuation

US$68.3

28.7% undervalued intrinsic discount

AnalystConsensusTarget Fair Value

Shared on01 Aug 25
Fair value Increased 8.76%

The consensus analyst price target for PTC Therapeutics has increased despite the company’s future P/E rising and net profit margin declining, indicating higher investor expectations for growth and raising the fair value estimate from $62.81 to $67.38. What's in the News FDA approved SEPHIENCE (sepiapterin) for treating phenylketonuria (PKU) in adults and children, with broad labeling and demonstrated efficacy and safety from Phase 3 and extension studies.

Shared on01 May 25
Fair value Decreased 55%

Shared on24 Apr 25

AnalystConsensusTarget made no meaningful changes to valuation assumptions.

Shared on17 Apr 25
Fair value Decreased 0.22%

AnalystConsensusTarget has decreased profit margin from 19.3% to 17.3% and increased future PE multiple from 33.6x to 37.3x.

Shared on09 Apr 25
Fair value Increased 0.11%

AnalystConsensusTarget made no meaningful changes to valuation assumptions.

Shared on02 Apr 25
Fair value Increased 118%

AnalystConsensusTarget made no meaningful changes to valuation assumptions.

Shared on26 Mar 25
Fair value Increased 2.45%

AnalystConsensusTarget made no meaningful changes to valuation assumptions.