U.S. Pharmaceuticals & Biotech High Growth Potential Companies

Zevra Therapeutics

Market Cap: US$469.0m

A commercial-stage company, focuses on addressing unmet needs for the treatment of rare diseases in the United States.

AVITA Medical

Market Cap: US$106.2m

Operates as a therapeutic acute wound care company in the United States, Japan, the European Union, Australia, and the United Kingdom.

Alnylam Pharmaceuticals

Market Cap: US$52.5b

Alnylam Pharmaceuticals, Inc. discovers, develops, and commercializes therapeutics based on ribonucleic acid interference.

Travere Therapeutics

Market Cap: US$3.1b

A biopharmaceutical company, identifies, develops, and delivers therapies to people living with rare kidney and metabolic diseases in the United States.

Ascendis Pharma

Market Cap: US$13.5b

Operates as a biopharmaceutical company that focuses on developing TransCon-based therapies for unmet medical needs in Denmark, rest of Europe, North America, and internationally.

Axsome Therapeutics

Market Cap: US$7.5b

A biopharmaceutical company, develops and delivers novel therapies for the management of central nervous system (CNS) disorders in the United States.

Madrigal Pharmaceuticals

Market Cap: US$13.0b

A biopharmaceutical company, focuses on delivering novel therapeutics for metabolic dysfunction-associated steatohepatitis (MASH) in the United States.

Caris Life Sciences

Market Cap: US$7.6b

An artificial intelligence TechBio company, provides molecular profiling services in the United States and internationally.

Arcutis Biotherapeutics

Market Cap: US$3.6b

A biopharmaceutical company, focuses on developing and commercializing treatments for dermatological diseases.

Marker Therapeutics

Market Cap: US$24.5m

A clinical-stage immuno-oncology company, engages in the development and commercialization of novel T cell-based immunotherapies for the treatment of hematological malignancies and solid tumor indications.

Evolus

Market Cap: US$456.3m

A performance beauty company, delivers products in the cash-pay aesthetic market in the United States, Canada, Europe, and Australia.

Mereo BioPharma Group

Market Cap: US$345.3m

A biopharmaceutical company, develops and commercializes therapeutics for the treatment of oncology and rare diseases in the United Kingdom, the United States, and internationally.

Alvotech

Market Cap: US$1.7b

Through its subsidiaries, develops and manufactures biosimilar medicines for patients worldwide.

Legend Biotech

Market Cap: US$4.1b

Through its subsidiaries, operates as a biopharmaceutical company that discovers, develops, manufactures, and commercializes novel cell therapies for oncology and other indications in the United States, China, and Europe.

Corcept Therapeutics

Market Cap: US$9.3b

Engages in discovery and development of medication for the treatment of severe endocrinologic, oncologic, metabolic, and neurologic disorders in the United States.

RenovoRx

Market Cap: US$35.2m

A clinical-stage biopharmaceutical company, engages in the developing of targeted combination therapies to enhance therapeutic outcomes for cancer patients undergoing treatment.

ARS Pharmaceuticals

Market Cap: US$1.0b

A biopharmaceutical company, develops and commercializes treatments for severe allergic reactions.

Aldeyra Therapeutics

Market Cap: US$273.1m

A biotechnology company, discovers and develops therapies designed to treat immune-mediated and metabolic diseases.

OS Therapies

Market Cap: US$63.7m

A clinical stage biopharmaceutical company, focuses on the identification, development, and commercialization of treatments for osteosarcoma and other solid tumors in the United States.

Achieve Life Sciences

Market Cap: US$247.0m

A late-stage pharmaceutical company, develops and commercializes cytisinicline for nicotine independence in Canada, the United States, and the United Kingdom.

Lineage Cell Therapeutics

Market Cap: US$402.3m

A clinical-stage biotechnology company, develops novel cell therapies for neurological and ophthalmic conditions in the United States and internationally.

Capricor Therapeutics

Market Cap: US$1.3b

A clinical-stage biotechnology company, engages in the development of transformative cell and exosome-based therapeutics for treating duchenne muscular dystrophy (DMD) and other diseases with unmet medical needs in the United States.

Evoke Pharma

Market Cap: US$23.6m

Operates as a specialty pharmaceutical company that focuses on the development and commercialization of drugs for the treatment of gastroenterological disorders and diseases.

LENZ Therapeutics

Market Cap: US$567.6m

Operates as a biopharmaceutical company that focuses on the development and commercialization of therapies to improve vision in the United States.

Soleno Therapeutics

Market Cap: US$2.8b

A clinical-stage biopharmaceutical company, focuses on the development and commercialization of novel therapeutics for the treatment of rare diseases.

ADMA Biologics

Market Cap: US$4.7b

A biopharmaceutical company, develops, manufactures, and markets specialty plasma-derived biologics for the treatment of immune deficiencies and infectious diseases in the United States and internationally.

UroGen Pharma

Market Cap: US$1.0b

Engages in the development and commercialization of solutions for urothelial and specialty cancers.

Pelthos Therapeutics

Market Cap: US$71.0m

A bio-pharmaceutical company, develops and commercializes therapeutic products to help patients with unmet treatment burdens.

Gossamer Bio

Market Cap: US$833.2m

A clinical-stage biopharmaceutical company, focuses on developing and commercializing seralutinib for the treatment of pulmonary arterial hypertension (PAH) in the United States.

Humacyte

Market Cap: US$245.3m

Engages in the development and manufacture of off-the-shelf, implantable, and bioengineered human tissues for the treatment of diseases and conditions across a range of anatomic locations in multiple therapeutic areas.

Codexis

Market Cap: US$150.8m

Provides enzymatic solutions for therapeutics manufacturing, leveraging its proprietary CodeEvolver technology platform to discover, develop, and enhance novel enzymes in the United States, Canada, Latin America, Europe, the Middle East, Africa, Australia, New Zealand, Southeast Asia, and China.

Syndax Pharmaceuticals

Market Cap: US$1.8b

A commercial-stage biopharmaceutical company, develops therapies for the treatment of cancer.

Eton Pharmaceuticals

Market Cap: US$447.9m

A pharmaceutical company, focuses on developing and commercializing treatments for rare diseases.

Viridian Therapeutics

Market Cap: US$3.1b

Engages in discovering, developing, and commercializing treatments for serious and rare diseases.

Citius Oncology

Market Cap: US$94.4m

Focuses on the development and commercialization of innovative targeted oncology therapies.

Longeveron

Market Cap: US$13.0m

A clinical stage biotechnology company, develops cellular therapies for aging-related and life-threatening conditions in the United States.