40 companies

Travere Therapeutics

Market Cap: US$2.6b

A biopharmaceutical company, identifies, develops, and delivers therapies to people living with rare kidney and metabolic diseases in the United States.

TVTX

US$28.47

7D

1.0%

1Y

47.7%

Axsome Therapeutics

Market Cap: US$8.5b

A biopharmaceutical company, develops and delivers novel therapies for the management of central nervous system (CNS) disorders in the United States.

AXSM

US$159.50

7D

-2.8%

1Y

33.5%

Madrigal Pharmaceuticals

Market Cap: US$9.9b

A biopharmaceutical company, focuses on delivering novel therapeutics for metabolic dysfunction-associated steatohepatitis (MASH) in the United States.

MDGL

US$431.53

7D

-0.8%

1Y

31.8%

Zevra Therapeutics

Market Cap: US$649.4m

A commercial-stage company, focuses on addressing unmet needs for the treatment of rare diseases in the United States.

ZVRA

US$10.41

7D

16.6%

1Y

31.4%

Insmed

Market Cap: US$31.0b

Develops and commercializes therapies for patients with serious and rare diseases in the United States, Europe, Japan, and internationally.

INSM

US$139.40

7D

-7.0%

1Y

88.3%

Rhythm Pharmaceuticals

Market Cap: US$6.4b

A commercial-stage biopharmaceutical company, focuses on the rare neuroendocrine diseases in the United States and internationally.

RYTM

US$90.02

7D

-1.1%

1Y

75.4%

Ardelyx

Market Cap: US$1.5b

Ardelyx, Inc. discovers, develops, and commercializes medicines to treat unmet medical needs in the United States and internationally.

ARDX

US$5.99

7D

-9.9%

1Y

10.1%

Pelthos Therapeutics

Market Cap: US$81.9m

A bio-pharmaceutical company, develops and commercializes therapeutic products to help patients with unmet treatment burdens.

PTHS

US$23.25

7D

1.0%

1Y

36.8%

Achieve Life Sciences

Market Cap: US$227.8m

A late-stage pharmaceutical company, develops and commercializes cytisinicline for nicotine independence in Canada, the United States, and the United Kingdom.

ACHV

US$4.38

7D

-4.4%

1Y

65.3%

Capricor Therapeutics

Market Cap: US$1.7b

A clinical-stage biotechnology company, engages in the development of transformative cell and exosome-based therapeutics for treating duchenne muscular dystrophy (DMD) and other diseases with unmet medical needs in the United States.

CAPR

US$33.57

7D

31.6%

1Y

156.8%

ARS Pharmaceuticals

Market Cap: US$879.8m

A biopharmaceutical company, develops and commercializes treatments for severe allergic reactions in the United States and internationally.

SPRY

US$8.38

7D

-7.3%

1Y

-31.9%

Corcept Therapeutics

Market Cap: US$3.6b

A biopharmaceutical company, engages in the discovery and development of medications to treat severe endocrinologic, oncologic, metabolic, and neurologic disorders in the United States.

CORT

US$33.74

7D

-5.5%

1Y

-38.7%

Alnylam Pharmaceuticals

Market Cap: US$42.8b

Alnylam Pharmaceuticals, Inc. discovers, develops, manufactures, and commercializes therapeutics based on ribonucleic acid interference in the United States, Europe, and internationally.

ALNY

US$320.43

7D

-2.1%

1Y

32.2%

CG Oncology

Market Cap: US$5.3b

A late-stage clinical biopharmaceutical company, develops and commercializes cretostimogene grenadenorepvec for patients with bladder cancer in the United States.

CGON

US$64.66

7D

5.0%

1Y

142.9%

CollPlant Biotechnologies

Market Cap: US$8.9m

A regenerative and aesthetic medicine company, focuses on three-dimensional (3D) bioprinting of tissues and organs, and medical aesthetics in the United States, Canada, Israel, Europe, and internationally.

CLGN

US$0.61

7D

-3.0%

1Y

-80.0%

Eton Pharmaceuticals

Market Cap: US$466.6m

A pharmaceutical company, focuses on developing and commercializing treatments for rare diseases.

ETON

US$18.09

7D

3.2%

1Y

22.4%

AC Immune

Market Cap: US$300.8m

A clinical stage biopharmaceutical company, discovers, designs, and develops medicines, and therapeutic and diagnostic products for the prevention and treatment of neurodegenerative diseases associated with protein misfolding.

ACIU

US$3.06

7D

7.7%

1Y

31.9%

Arcutis Biotherapeutics

Market Cap: US$3.0b

A biopharmaceutical company, focuses on developing and commercializing treatments for dermatological diseases.

ARQT

US$23.95

7D

-0.7%

1Y

58.0%

Viridian Therapeutics

Market Cap: US$3.0b

Engages in discovering, developing, and commercializing treatments for serious and rare diseases.

VRDN

US$28.62

7D

-5.8%

1Y

71.9%

Kiniksa Pharmaceuticals International

Market Cap: US$3.6b

A biopharmaceutical company, develops and commercializes medical therapies in the United States, the United Kingdom, and internationally.

KNSA

US$46.31

7D

-2.0%

1Y

105.8%

Stoke Therapeutics

Market Cap: US$2.2b

An early-stage biopharmaceutical company, engages in the development of treatments for severe genetic diseases by upregulating protein expression.

STOK

US$37.94

7D

10.2%

1Y

345.3%

Belite Bio

Market Cap: US$6.8b

A clinical stage biopharmaceutical drug development company, engages in the research and development of novel therapeutics targeting retinal degenerative eye diseases with unmet medical needs in the United States.

BLTE

US$173.75

7D

-2.3%

1Y

150.1%

NewAmsterdam Pharma

Market Cap: US$3.6b

A late-stage biopharmaceutical company, develops therapies to enhance patient care in populations with cardiometabolic disease.

NAMS

US$31.35

7D

0.5%

1Y

34.2%

BeOne Medicines

Market Cap: US$33.9b

An oncology company, engages in discovering and developing various treatments for cancer patients in the United States, China, Europe, and internationally.

ONC

US$298.91

7D

-0.04%

1Y

19.6%

Unicycive Therapeutics

Market Cap: US$149.4m

A clinical-stage biotechnology company, identifies, develops, and commercializes therapies to address unmet medical needs in the United States.

New

UNCY

US$7.04

7D

-0.4%

1Y

19.4%

Liquidia

Market Cap: US$3.4b

A biopharmaceutical company, develops, manufactures, and commercializes various products for rare cardiopulmonary diseases in the United States.

New

LQDA

US$38.56

7D

12.2%

1Y

165.9%

Praxis Precision Medicines

Market Cap: US$8.3b

A clinical-stage biopharmaceutical company, engages in the development of therapies for central nervous system (CNS) disorders characterized by neuronal excitation-inhibition imbalance in the United States.

PRAX

US$296.97

7D

-4.4%

1Y

696.4%

Krystal Biotech

Market Cap: US$7.6b

A commercial-stage biotechnology company, discovers, develops, manufactures, and commercializes genetic medicines to treat diseases with high unmet medical needs in the United States.

New

KRYS

US$255.00

7D

-3.8%

1Y

42.9%

Gyre Therapeutics

Market Cap: US$738.0m

A pharmaceutical company, engages in the development and commercialization of small-molecule, anti-inflammatory, and anti-fibrotic drugs targeting organ fibrosis.

GYRE

US$8.33

7D

0.6%

1Y

-28.6%

Mirum Pharmaceuticals

Market Cap: US$5.5b

A biopharmaceutical company, focuses on the development and commercialization of novel therapies for debilitating rare and orphan diseases.

MIRM

US$91.75

7D

-1.4%

1Y

103.8%

Fortress Biotech

Market Cap: US$104.3m

A biopharmaceutical company, engages in the development and commercialization of biopharmaceutical products.

FBIO

US$3.22

7D

3.9%

1Y

86.1%

Amicus Therapeutics

Market Cap: US$4.5b

A biotechnology company, focuses on discovering, developing, and delivering novel medicines for rare diseases in the United States and internationally.

FOLD

US$14.37

7D

0.3%

1Y

61.6%

Arcellx

Market Cap: US$6.7b

Together with its subsidiary, engages in the development of various immunotherapies for patients with cancer and other incurable diseases in the United States.

ACLX

US$114.36

7D

0.05%

1Y

57.3%

Benitec Biopharma

Market Cap: US$420.3m

A clinical-stage biotechnology company, focuses on the development of novel genetic medicines.

BNTC

US$12.28

7D

12.6%

1Y

-15.3%

Journey Medical

Market Cap: US$271.0m

Focuses on the development and commercialization of pharmaceutical products for the treatment of dermatological conditions in the United States.

DERM

US$8.18

7D

1.7%

1Y

54.0%

Prothena

Market Cap: US$525.9m

A late-stage clinical biotechnology company, focuses on discovery and development of novel therapies to treat diseases caused by protein dysregulation.

New

PRTA

US$9.58

7D

-2.8%

1Y

-30.9%

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